
Yesterday, it could take 10yrs and hundreds of millions of dollars to develop a treatment with a 5% chance of success.
Today, we can design, develop, and treat a child with a rare genetic disease in as little as a year. We want to do this at scale.
Our Strategy
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Built Around Patients
We build medicines, technologies, systems, and efficiencies with urgency that we believe will directly impact patients access to treatments. Time = Life.
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Antisense Oligonucleotides
We utilize a proven genetic medicine platform that has the characteristics of highly targeted, rapid development, and affordable manufacturing.
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AI
We leverage the power of AI/ML to target the right genes, design the better medicines, and reduce the time in pre clinical and clinical development